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Clinical Trials

Below is a list of active clinical trials worldwide which involve patients with inherited bleeding disorders. The link from each study title will take you to ClinicalTrials.gov which gives you more information about the trial.
To see a list of trials for a particular bleeding disorder use the drop-down list below to select the condition you're interested in. A new window will open up with a list of trials for this condition only.

Please select the category:
PRIOR Study (Pre-eclampsia Risk In Oocyte Recipients)
Conditions: Pre-eclampsia; Oocyte Donation; Pre-Eclampsia; Complicating Pregnancy; Pre-Eclampsia; Mild; Pre-Eclampsia, Severe; Pre-eclampsia or Eclampsia With Pre-existing Hypertension; ART; Neonatal Morbidity; Neonatal Mortality; Placental Abruption; Gestational Diabetes; Preterm Labor; Post-partum Hemorrhage (PPH); Intrauterine Growth Restriction (IUGR); Hypertensive Disorders of Pregnancy
Sponsors: Copenhagen University Hospital, Hvidovre; Ferring Pharmaceuticals; Gedeon Richter Ltd.
Recruiting
Feasibility and Safety of Blood-Flow-Restriction Training in Patients With Hemophilia
Conditions: Hemophilia
Interventions: Device: Control; Device: BFR Exercise (50% of the LOP) while Leg Press Exercise (4 Sets, All out)
Sponsors: University Hospital, Bonn
Enrolling by invitation
Link Between Abnormal Bleeding and Coagulation Disorders in Noonan Syndromes
Conditions: Noonan Syndrome
Interventions: Other: Reuse of routine clinical and biological data
Sponsors: University Hospital, Bordeaux
Not yet recruiting
A Trial of TER-1754 in Patients With Hereditary Hemorrhagic Telangiectasia
Conditions: Hereditary Hemorrhagic Telangiectasia (HHT)
Interventions: Drug: TER-1754; Drug: Placebo; Drug: TER-1754
Sponsors: Terremoto Biosciences Inc.
Not yet recruiting
Anakinra Pilot 2 - A Study to Optimise Dose and Route of Administration of Anakinra in Preterm Infants
Conditions: Premature Infants; Very Premature Infants; Inflammation
Interventions: Drug: Anakinra (Kineret®)
Sponsors: Monash Medical Centre; Monash University; Hudson Institute of Medical Research; Liggins Institute; Starship Children's Hospital of New Zealand
Recruiting
Oral Health Related Quality of Life of Children With Amelogenesis Imperfecta
Conditions: Amelogenesis Imperfecta
Interventions: Procedure: Veneers
Sponsors: Istanbul University
Active, not recruiting
Ruxolitinib-Enhanced Haplo HCT for Children and Young Adults With Sickle Cell Disease
Conditions: Sickle Cell Disease; Hematopoetic Stem Cell Transplant; Haploidentical Hematopoietic Stem Cell Transplant; Haploidentical Stem Cell Transplantation; Graft Failure
Interventions: Drug: Ruxolitinib
Sponsors: University of Colorado, Denver; Children's Healthcare of Atlanta; Emory University; Incyte Corporation
Not yet recruiting
Early Hydrocortisone Versus Regular Treatment in Shock in Extremely Preterm Neonates - an Open Randomized Controlled Trial
Conditions: Shock; Preterm Birth Complication; Preterm Intraventricular Hemorrhage; Asphyxia Perinatal; Distress Respiratory Syndrome; Hyperglycaemia (Non Diabetic); Neonatal Sepsis, Early-Onset; Neonatal Sepsis, Late-Onset; NEC - Necrotizing Enterocolitis; Patent Ductus Arteriosus in Preterm Infants; Intestinal Perforation
Interventions: Drug: Intravascular Hydrocortisone (stress dosage): 1 mg/k/dose each 8 hours for 5 days; Other: Vasoactive drug therapies
Sponsors: Coordinación de Investigación en Salud, Mexico; Instituto Mexicano del Seguro Social
Active, not recruiting
Balance Evaluation in Adult Hemophilia
Conditions: Postural Balance
Interventions: Diagnostic Test: Postural balance assessment
Sponsors: Ayse Merve TAT
Completed