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Clinical Trials

Below is a list of active clinical trials worldwide which involve patients with inherited bleeding disorders. The link from each study title will take you to ClinicalTrials.gov which gives you more information about the trial.
To see a list of trials for a particular bleeding disorder use the drop-down list below to select the condition you're interested in. A new window will open up with a list of trials for this condition only.

Please select the category:
Identification of New Biomarkers in Haemophilic Arthropathy Through Transcriptome Analysis
Conditions: Hemophilia A and B
Interventions: Procedure: Surgery
Sponsors: Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico
Recruiting
Tight Control of Treatment Adherence and Efficacy by Telemedicine for an Improved Personalized Management of Patients With Hemophilia
Conditions: Hemophilia
Interventions: Other: TEMPO
Sponsors: Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico
Recruiting
Elevated Midline Positioning During Diaper Change in Preterm Infants
Conditions: Infant, Premature, Diseases; Premature Birth of Newborn; Pain
Interventions: Other: 30-Degree Elevated Midline Positioning; Other: Standard Lateral Position Diaper Change
Sponsors: Akdeniz University
Not yet recruiting
Multicomponent Pain Self-Management in Adults With Haemophilic Arthropathy
Conditions: Hemophilic Arthropathy; Chronic Pain; Hemophilia A; Hemophilia B
Interventions: Other: Multicomponent pain self-management programme
Sponsors: Investigación en Hemofilia y Fisioterapia
Not yet recruiting
A Study to Learn About the Study Medicine (Called Marstacimab) in People With Hemophilia A or B
Conditions: Hemophilia
Interventions: Drug: Marstacimab
Sponsors: Pfizer
Not yet recruiting
Validity and Reliability of the Figure-of-Eight Walking and Weight-Bearing Lunge Tests in Hemophilia
Conditions: Hemophilia
Sponsors: Yuzuncu Yil University
Recruiting
Low-Dose Sirolimus for the Treatment of RUNX1 Familial Platelet Disorder
Conditions: Familial Platelet Disorder With Associated Myeloid Malignancy
Interventions: Procedure: Biospecimen Collection; Procedure: Bone Marrow Aspiration; Procedure: Bone Marrow Biopsy; Other: Questionnaire Administration; Drug: Sirolimus
Sponsors: OHSU Knight Cancer Institute; National Cancer Institute (NCI); Oregon Health and Science University; M.D. Anderson Cancer Center
Recruiting
Topical Tranexamic Acid Spray Versus No Spray on Postoperative Outcomes Following Mesh Repair of Umbilical Hernia
Conditions: Umbilical Hernia Repair
Interventions: Drug: Topical Tranexamic Acid Spray; Drug: No Topical Tranexamic acid
Sponsors: Dr Mudassar Saeed Pansota
Not yet recruiting
Early Postoperative Triple Targeted Therapy in Patients With CHD-PAH in the "Grey Zone"
Conditions: Congenital Heart Disease, Pulmonary Hypertension
Interventions: Drug: Control group (ambrisentan plus tadalafil or macitentan plus tadalafil); Drug: Treatment group (ambrisentan plus tadalafil plus treprostinil or macitentan plus tadalafil plus treprostinil)
Sponsors: China National Center for Cardiovascular Diseases
Completed