Clinical Trials

Below is a list of active clinical trials worldwide which involve patients with inherited bleeding disorders. The link from each study title will take you to ClinicalTrials.gov which gives you more information about the trial.
To see a list of trials for a particular bleeding disorder use the drop-down list below to select the condition you're interested in. A new window will open up with a list of trials for this condition only.

A Trial to Learn if REGV131-LNP1265 is Safe and Works to Help the Body Make Clotting Factor in Pediatric, Adolescent and Adult Patients With Hemophilia B Conditions: Hemophilia B Interventions: Drug: REGV131; Drug: LNP1265 Sponsors: Regeneron Pharmaceuticals; Intellia Therapeutics Not yet recruiting

Case and Use Scenario Study to Gain Knowledge on the User Needs for a Medical Device for Hemophilia A Monitoring Conditions: Hemophilia A Interventions: Other: Case scenarios - questionnaire; Other: Case scenarios - Focus groups; Other: Use scenarios - Usability test; Other: Use scenarios - interview Sponsors: Enzyre B.V.; Indiana Hemophilia & Thrombosis Center Not yet recruiting

Phase 1b Trial of RAY121 in Immunological Diseases (RAINBOW Trial) Conditions: Antiphospholipid Syndrome (APS); Bullous Pemphigoid (BP); Behçet's Syndrome (BS); Dermatomyositis (DM); Immune-mediated Necrotizing Myopathy (IMNM); Immune Thrombocytopenia (ITP) Interventions: Drug: RAY121 Sponsors: Chugai Pharmaceutical Not yet recruiting