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Clinical Trials

Below is a list of active clinical trials worldwide which involve patients with inherited bleeding disorders. The link from each study title will take you to ClinicalTrials.gov which gives you more information about the trial.
To see a list of trials for a particular bleeding disorder use the drop-down list below to select the condition you're interested in. A new window will open up with a list of trials for this condition only.

Please select the category:
ASO Treatment for Syndromic Craniosynostoses
Conditions: Craniosynostoses; Crouzon Syndrome; Saethre Chotzen Syndrome; Muenke Syndrome; Pfeiffer Syndrome; Apert Syndrome
Interventions: Genetic: Design of patient specific ASO
Sponsors: Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Not yet recruiting
RADIOLOGICAL AND CLINICAL EVALUATION OF RENAL EMBOLIZATION USING EVOH IN DIALYSIS PATIENTS WITH AUTOSOMAL DOMINANT POLYCYSTIC KIDNEY DISEASE: A PROSPECTIVE LONGITUDINAL OBSERVATIONAL STUDY
Conditions: Autosomal Dominant Polycystic Kidney Disease (ADPKD)
Sponsors: Fondazione IRCCS Policlinico San Matteo di Pavia
Recruiting
Ibuprofen vs Expectant Management for hsPDA in Preterm Infants: Retrospective Cohort
Conditions: Patent Ductus Arteriosus; Infant, Premature
Interventions: Drug: Ibuprofen
Sponsors: Shengjing Hospital
Completed
Retinoblastoma Consolidation in Egyptians
Conditions: Retinoblastoma
Interventions: Procedure: transpupillary thermotherapy; Procedure: Cryotherapy; Radiation: Brachytherapy
Sponsors: Assiut University
Not yet recruiting
Joint Health, Balance and Quality of Life in Adults With Hemophilia A
Conditions: Hemophilia A
Sponsors: Yuzuncu Yil University
Recruiting
Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)
Conditions: Tetraplegia/Tetraparesis; Amyotrophic Lateral Sclerosis (ALS); Muscular Disorders, Atrophic; Brain Stem Stroke; Spinal Cord Injuries (SCI); Muscular Dystrophies; Muscular Atrophy, Progressive; Pontine Hemorrhage; Pontine Infarction
Interventions: Device: INTENT Neural Interface System
Sponsors: Johns Hopkins University; Blackrock Neurotech; JHU Applied Physics Laboratory; Kennedy Krieger Institute, Baltimore, MD
Recruiting
LLM-Based Intelligent Health Management Assistant in Life-Cycle Health Management of Cardiac Surgery Patients
Conditions: Coronary Artery Bypass Grafting; Heart Valve Disease; Aortic Aneurysm; Aortic Dissection; Congenital Heart Disease; Cardiac Surgical Procedures
Interventions: Other: LLM-Based Intelligent Health Management Assistant
Sponsors: Beijing Anzhen Hospital
Not yet recruiting
Central Pain Mechanisms and Clinical and Psychological Factors Associated With Pain Interference in Daily Life in Adults With Hemophilia and Hemophilic Arthropathy
Conditions: Hemophilia
Sponsors: Investigación en Hemofilia y Fisioterapia
Not yet recruiting