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Clinical Trials

Below is a list of active clinical trials worldwide which involve patients with inherited bleeding disorders. The link from each study title will take you to ClinicalTrials.gov which gives you more information about the trial.
To see a list of trials for a particular bleeding disorder use the drop-down list below to select the condition you're interested in. A new window will open up with a list of trials for this condition only.

Please select the category:
Effects of Non-Surgical Periodontal Treatment on Inflammatory and Bone Markers in Periodontitis Patients
Conditions: Periodontitis (Stage 3)
Interventions: Procedure: Scaling and Root Planing (SRP)
Sponsors: Saglik Bilimleri Universitesi
Not yet recruiting
Quality of Life in Pediatric Participants With HHT
Conditions: Hereditary Haemorrhagic Telangiectasia (HHT)
Sponsors: Ashley Nelson
Not yet recruiting
Autus Valve Continued Access Study (CAS)
Conditions: Congenital Heart Disease
Interventions: Device: Pulmonary Valve Replacement Surgery
Sponsors: Autus Valve Technologies, Inc.
Not yet recruiting
EPOCH-Economics and Patient Outcomes in China in Haemophilia
Conditions: Hemophilia
Sponsors: Institute of Hematology & Blood Diseases Hospital, China; EPOCH Study, Ltd.
Active, not recruiting
3D Ultrasound in Hemophilic Ankles
Conditions: Hemophilia
Interventions: Device: Mechanical Ultrasound
Sponsors: The Hospital for Sick Children; Western University, Canada
Not yet recruiting
Post Approval Observational Study to Learn More About How Safe Octocog Alfa is and How Well it Works in Patients With Severe Hemophilia A in India
Conditions: Severe Hemophilia A
Interventions: Drug: Octocog alfa
Sponsors: Bayer
Not yet recruiting
Efficacy and Tolerance of Treatment With Bevacizumab for Severe Liver Involvement With High Cardiac Output in Hereditary Hemorrhagic Telangiectasia Within the French Hereditary Hemorrhagic Telangiectasia Network
Conditions: Hereditary Hemorrhagic Telangiectasia (HHT); Pulmonary Hypertension; Bevacizumab
Interventions: Drug: Bevacizumab
Sponsors: Poitiers University Hospital
Enrolling by invitation
Can Betamethasone Given After Birth Help Extremely Premature Babies Come Off Breathing Support Safely and Effectively?
Conditions: Respiratory Distress Syndrome (RDS); Bronchopulmonary Dysplasia (BPD)
Interventions: Drug: Betamethasone
Sponsors: Khang Nguyen
Not yet recruiting