Clinical Trials

Below is a list of active clinical trials worldwide which involve patients with inherited bleeding disorders. The link from each study title will take you to ClinicalTrials.gov which gives you more information about the trial.
To see a list of trials for a particular bleeding disorder use the drop-down list below to select the condition you're interested in. A new window will open up with a list of trials for this condition only.

EPOCH-Economics and Patient Outcomes in China in Haemophilia Conditions: Hemophilia Sponsors: Institute of Hematology & Blood Diseases Hospital, China; EPOCH Study, Ltd. Active, not recruiting

3D Ultrasound in Hemophilic Ankles Conditions: Hemophilia Interventions: Device: Mechanical Ultrasound Sponsors: The Hospital for Sick Children; Western University, Canada Not yet recruiting

Efficacy and Tolerance of Treatment With Bevacizumab for Severe Liver Involvement With High Cardiac Output in Hereditary Hemorrhagic Telangiectasia Within the French Hereditary Hemorrhagic Telangiectasia Network Conditions: Hereditary Hemorrhagic Telangiectasia (HHT); Pulmonary Hypertension; Bevacizumab Interventions: Drug: Bevacizumab Sponsors: Poitiers University Hospital Enrolling by invitation

Post Approval Observational Study to Learn More About How Safe Octocog Alfa is and How Well it Works in Patients With Severe Hemophilia A in India Conditions: Severe Hemophilia A Interventions: Drug: Octocog alfa Sponsors: Bayer Not yet recruiting

Can Betamethasone Given After Birth Help Extremely Premature Babies Come Off Breathing Support Safely and Effectively? Conditions: Respiratory Distress Syndrome (RDS); Bronchopulmonary Dysplasia (BPD) Interventions: Drug: Betamethasone Sponsors: Khang Nguyen Not yet recruiting

Efficacy and Safety Evaluation Study of SCT800 in Previously Untreated Hemophilia A Patients. Conditions: Haemophilia A Interventions: Drug: SCT800 prophylaxis and treatment for bleeding events Sponsors: Sinocelltech Ltd. Recruiting

Real-World Joint Outcomes After Selective Transition to Low-Dose Emicizumab in Pediatric Hemophilia A Conditions: Hemophilia A Patient Interventions: Drug: Switching to low dose emicizumab Sponsors: Chulalongkorn University Active, not recruiting

A Study to Learn More About the Treatment of People With Congenital Thrombotic Thrombocytopenic Purpura (cTTP) Who Received Recombinant ADAMTS13 (rADAMTS13) as Part of the Early Access Program Conditions: Thrombotic Thrombocytopenic Purpura (TTP) Interventions: Other: No Intervention Sponsors: Takeda Not yet recruiting

Retinopathy of Prematurity - Visual Function and Retinal Structure Conditions: Retinopathy of Prematurity (ROP); Prematurity Complications; Cerebral Visual Impairment; Visual Field Defect Sponsors: Oslo University Hospital Not yet recruiting